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Distinct drugs in development (Preclinical–Phase 3)
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Distinct diseases across all programs
Clinical Trials↗
All sponsored trials (all statuses)
Activity
Last 14 days
Home Monitoring of Adult Patients With SMA: a Pilot Multicenter Validation Study
Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers
A Prospective, Longitudinal, Interventional Natural History Study of Children With LAMA2-related Dystrophies
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Data sources: ClinicalTrials.gov (NIH) · OpenFDA (FDA) · ChEMBL (EMBL-EBI) · Open Targets (EBI/Sanger) · MedlinePlus (NIH) · PubMed (NIH) · SEC EDGAR (SEC)