Soliris/Ultomiris is one of 32 small molecule programs targeting Paroxysmal Nocturnal Hemoglobinuria. It is currently in Preclinical.
Indications
Total Trials
Active Trials
Competitors
Pipeline
Competition
39 competitors in Paroxysmal Nocturnal Hemoglobinuria
VEOPOZ
Fabhalta
Cemdisiran
Empaveli
Neupogen
Cytoxan
PIASKY
LNP023
Glucocorticoids
LFG316
Ranked by pipeline maturity and clinical activity. Current drug highlighted in teal.
Timeline
Clinical
Sources
Details