VivoSeq
Metabolic & Endocrine

Glycogen Storage Disease Due to Acid Maltase Deficiency

8

Pipeline Programs

0

Active Trials

7

Companies Involved

Glycogen storage disease due to acid maltase deficiency is an early-stage landscape with 8 programs across 7 companies. The most active players are Roche, Glaxo Dba Glaxosmithkline, Prism Pharmaceuticals. 5 therapies are approved.

Pipeline Metrics

Competitive Density

33/100

Pipeline Velocity

0/100

Mech. Concentration

14/100

Completion Rate

N/A

Attrition Rate

N/A

Competitive Landscape

Bubble size = clinical trials

Approved
Phase 3
Phase 2
Phase 1
Preclinical

Programs by Phase

Modality Breakdown

63%

Small molecule

5 of 8 classified programs — the dominant modality here.

38%ALL OTHERSProtein / enzyme225%Monoclonal antibody113%

Small molecule leads; the ring shows all 8 classified programs, each share of the total. Modality classified for 100% of 8 pipeline programs.

Data sources: ClinicalTrials.gov (NIH) · OpenFDA (FDA) · ChEMBL (EMBL-EBI) · Open Targets (EBI/Sanger) · MedlinePlus (NIH) · PubMed (NIH) · SEC EDGAR (SEC)