disease modifying treatments is one of 13 small molecule programs targeting Spinal Muscular Atrophy. It is currently in Preclinical.
Indications
Total Trials
Active Trials
Competitors
Pipeline
Competition
14 competitors in Spinal Muscular Atrophy
Spinraza
Evrysdi
Prilosec
Amondys 45
Onasemnogene Abeparvovec
Salanersen
Apitegromab
Taldefgrobep Alfa
Vesemnogene Lantuparvovec
NMD670
Ranked by pipeline maturity and clinical activity. Current drug highlighted in teal.
Clinical
Sources
Details