disease modifying treatments is one of 28 small molecule programs targeting Spinal Muscular Atrophy. It is currently in Preclinical.
Indications
Total Trials
Active Trials
Competitors
Pipeline
Competition
35 competitors in Spinal Muscular Atrophy
Evrysdi
Spinraza
Prilosec
Amondys 45
Depakote
Droxia
Celebrex
Rilutek
Onasemnogene Abeparvovec
RO7204239
Ranked by pipeline maturity and clinical activity. Current drug highlighted in teal.
Clinical
Sources
Details