rhASM is one of 7 small molecule programs targeting Niemann-Pick disease. It is currently in Phase 1.
Indications
Total Trials
Active Trials
Competitors
Pipeline
Competition
8 competitors in Niemann-Pick Disease
Cytoxan
Busulfex
N-Acetyl Cyteien
Zolinza
IB1001
VTS-270
rhASM
Ranked by pipeline maturity and clinical activity. Current drug highlighted in teal.
Clinical
Sources